Publication Topic

gene-replacement therapy (2 POSTS)

2020 (1 POST)

Dean R, Miller B, Arjunji R, Feltner DE, Sproule DM, Jensen I, Dabbous O. Cost-utility analysis of single dose gene-replacement therapy for spinal muscular atrophy type 1 compared to chronic nusinersen treatment in Japan. Abstract PMU36. ISPOR 2020.

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2019 (1 POST)

Malone D, Miller B, Dean R, Arjunji R, Jensen IS, Maru B, et al. Use of single dose gene-replacement therapy for the treatment of spinal muscular atrophy type 1: A United States payer budget impact analysis. ISPOR 2019.